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Niemann-Pick-Disease Pipeline Outlook, Clinical Trials, FDA Approvals, and Companies 2024 (Updated)

04-25-2024 02:49 AM CET | Health & Medicine

Press release from: DelveInsight Business Research LLP

Niemann-Pick-Disease Pipeline

Niemann-Pick-Disease Pipeline

DelveInsight's, "Niemann-Pick-Disease Pipeline Insight 2024" report provides comprehensive insights about 20+ companies and 20+ pipeline drugs in the Niemann-Pick-Disease pipeline landscape. It covers the Niemann-Pick-Disease pipeline drug profiles, including clinical and nonclinical stage products. It also covers the therapeutics assessment by product type, stage, route of administration, and molecule type. It further highlights the inactive pipeline products in this space.

Key Takeaways from the Niemann-Pick-Disease Pipeline Report
• DelveInsight's Niemann-Pick-Disease pipeline report depicts a robust space with 20+ active players working to develop 20+ pipeline therapies for Niemann-Pick-Disease treatment.
• The leading companies working in the Niemann-Pick-Disease Market include Orphazyme, Cyclo Therapeutics, Mandos LLC, IntraBio, E-scape Bio, Scenic Biotech, Synaptogenix, Evox Therapeutics, StrideBio, SOM Biotech, ENDECE, Oraxion Therapeutics, Polaryx Therapeutics, and others.
• Promising Niemann-Pick-Disease Pipeline Therapies in the various stages of development include N-Acetyl-L-Leucine, Hydroxypropyl-beta-cyclodextrin, arimoclomol, IB1001, and others.
• April 2024: Sanofi- A Prospective Observational Study to Assess the Long-term Safety and Immunogenicity of Olipudase Alfa Therapy During Routine Clinical Care in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency.

Request a sample and discover the recent advances in Niemann-Pick-Disease Treatment Drugs @ Niemann-Pick-Disease Pipeline Report- https://www.delveinsight.com/report-store/niemann-pick-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

In the Niemann-Pick-Disease pipeline report, detailed description of the drug is given which includes mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, Niemann-Pick-Disease collaborations, licensing, mergers and acquisition, funding, designations and other product related details.

Niemann-Pick-Disease Overview
Niemann-Pick Diseases (NPD) include heterogeneous groups of autosomal recessive lysosomal lipid storage disorders, with common features of hepatosplenomegaly and sphingomyelin storage in reticuloendothelial and parenchymal tissues, with or without neurological involvement. Niemann-Pick Disease (NPD) is classified as Niemann-Pick Disease type A, Niemann-Pick Disease type B, and Niemann-Pick Disease type C.

Find out more about Niemann-Pick-Disease Therapeutics Assessment @ Niemann-Pick-Disease Preclinical and Discovery Stage Products- https://www.delveinsight.com/sample-request/niemann-pick-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Niemann-Pick-Disease Emerging Drugs Profile
• Arimoclomol: Orphazyme
• Trappsol Cyclo: Cyclo Therapeutics
• VTS-270: Mandos LLC
• ESB1609: E-scape Bio

Niemann-Pick-Disease Pipeline Therapeutics Assessment
There are approx. 20+ key companies which are developing the Niemann-Pick-Disease therapies. The Niemann-Pick-Disease companies which have their Niemann-Pick-Disease drug candidates in the most advanced stage, i.e. Pre-Registration, Orphazyme.

Learn more about the emerging Niemann-Pick-Disease Pipeline Therapies @ Niemann-Pick-Disease Clinical Trials Assessment- https://www.delveinsight.com/sample-request/niemann-pick-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Scope of the Niemann-Pick-Disease Pipeline Report
• Coverage- Global
• Niemann-Pick-Disease Therapeutic Assessment by Product Type: Mono, Combination, Mono/Combination
• Niemann-Pick-Disease Therapeutic Assessment by Clinical Stages: Discovery, Pre-clinical, Phase I, Phase II, Phase III
• Niemann-Pick-Disease Companies- Orphazyme, Cyclo Therapeutics, Mandos LLC, IntraBio, E-scape Bio, Scenic Biotech, Synaptogenix, Evox Therapeutics, StrideBio, SOM Biotech, ENDECE, Oraxion Therapeutics, Polaryx Therapeutics, and others.
• Niemann-Pick-Disease Pipeline Therapies- N-Acetyl-L-Leucine, Hydroxypropyl-beta-cyclodextrin, arimoclomol, IB1001, and others.

Dive deep into rich insights for new drugs for Niemann-Pick-Disease treatment, Visit @ Niemann-Pick-Disease Market Drivers and Barriers, and Future Perspective- https://www.delveinsight.com/sample-request/niemann-pick-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

Table of Content
1. Introduction
2. Executive Summary
3. Niemann-Pick-Disease: Overview
4. Pipeline Therapeutics
5. Therapeutic Assessment
6. Niemann-Pick-Disease- DelveInsight's Analytical Perspective
7. Late Stage Products (Pre-Registration)
8. Arimoclomol: Orphazyme
9. Drug profiles in the detailed report…..
10. Mid Stage Products (Phase II)
11. Drug name : Company name
12. Drug profiles in the detailed report…..
13. Early Stage Products (Phase I)
14. ESB1609: E-scape Bio
15. Drug profiles in the detailed report…..
16. Preclinical and Discovery Stage Products
17. Drug name : Company name
18. Drug profiles in the detailed report…..
19. Inactive Products
20. Niemann-Pick-Disease Key Companies
21. Niemann-Pick-Disease Key Products
22. Niemann-Pick-Disease- Unmet Needs
23. Niemann-Pick-Disease- Market Drivers and Barriers
24. Niemann-Pick-Disease- Future Perspectives and Conclusion
25. Niemann-Pick-Disease Analyst Views
26. Niemann-Pick-Disease Key Companies
27. Appendix

For further information on the Niemann-Pick-Disease pipeline therapeutics, reach out to Niemann-Pick-Disease Unmet Needs and Analyst Views- https://www.delveinsight.com/sample-request/niemann-pick-disease-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr

List of Important Links-
http://demo.advised360.com/read-blog/154799
https://thehealthbridges.com/read-blog/19127
https://app.talkshoe.com/user/joneswilliam/about#google_vignette
https://www.vaca-ps.org/blogs/142022/The-Evolving-Landscape-of-Healthcare-Business-Consulting-Services
https://www.anobii.com/en/01d38d0b9694756e64/profile/activity
https://myanimelist.net/profile/dennydonesgerman
https://forum.pivx.org/threads/healthcare-business-consulting-services-navigating-complexity-in-modern-healthcare.2035/
https://pubhtml5.com/homepage/npvs/
https://b31.org.uk/author/anniesmith9/
https://fairygodboss.com/users/profile/Ix-vMa09gj/Annie-Smith
https://forum.completefrance.com/index.php?/topic/71194-key-areas-of-focus-in-healthcare-consulting-services/
https://educatorpages.com/site/kelleadvin/pages/blog?
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About Us

DelveInsight is a leading healthcare-focused market research and consulting firm that provides clients with high-quality market intelligence and analysis to support informed business decisions. With a team of experienced industry experts and a deep understanding of the life sciences and healthcare sectors, we offer customized research solutions and insights to clients across the globe. Connect with us to get high-quality, accurate, and real-time intelligence to stay ahead of the growth curve.

Company Name: DelveInsight Business Research LLP
Contact Person: Yash Bhardwaj
Email: ybhardwaj@delveinsight.com
Phone: 9650213330
Address: 304 S. Jones Blvd #2432
City: Las Vegas
State: NV
Country: United States
Website:- https://www.delveinsight.com/

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