Press release
Metachromatic Leukodystrophy Pipeline, FDA Approvals, Clinical Trials Developments and Companies 2024 (Updated)
Metachromatic Leukodystrophy Pipeline
Key Takeaways from the Metachromatic Leukodystrophy Pipeline Report
• DelveInsight's Metachromatic Leukodystrophy pipeline report depicts a robust space with 6+ active players working to develop 6+ pipeline therapies for Metachromatic Leukodystrophy treatment.
• The leading companies working in the Metachromatic Leukodystrophy Market include Takeda, Denali Therapeutics, Orchard Therapeutics, Homology Medicines, Passage Bio, ArmaGen Technologies, and others.
• Promising Metachromatic Leukodystrophy Pipeline Therapies in the various stages of development include SHP611, HGT-1110, OTL-200, rhARSA, MGTA-456, and others.
• January 2024:- Orchard Therapeutics- An Open Label, Non-randomized Trial to Evaluate the Safety and Efficacy of a Single Infusion of OTL-200 in Patients With Late Juvenile (LJ) Metachromatic Leukodystrophy (MLD). OTL-200 is a cryopreserved dispersion for infusion containing autologous CD34+ cell enriched population that contains haematopoietic stem and progenitor cells (HSPC) transduced ex vivo using a lentiviral vector encoding the human arylsulfatase A (ARSA) gene. MLD is an autosomal recessive lysosomal storage disorder (LSD) characterized by severe and progressive demyelination affecting the central and peripheral nervous system.
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In the Metachromatic Leukodystrophy pipeline report, detailed description of the drug is given which includes mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, Metachromatic Leukodystrophy collaborations, licensing, mergers and acquisition, funding, designations and other product related details.
Metachromatic Leukodystrophy Overview
Metachromatic leukodystrophy (MLD) is a rare hereditary disease characterized by accumulation of fats called sulfatides. This causes the destruction of the protective fatty layer (myelin sheath) surrounding the nerves in both the central nervous system and the peripheral nervous system. There are three types of MLD based on the age symptoms appear: late-infantile MLD, juvenile MLD, and adult MLD.
Find out more about Metachromatic Leukodystrophy Therapeutics Assessment @ Metachromatic Leukodystrophy Preclinical and Discovery Stage Products- https://www.delveinsight.com/sample-request/metachromatic-leukodystrophy-mld-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr
Metachromatic Leukodystrophy Emerging Drugs Profile
• OTL-200: Orchard Therapeutics
• TAK-611: Takeda
Metachromatic Leukodystrophy Pipeline Therapeutics Assessment
There are approx. 6+ key companies which are developing the Metachromatic Leukodystrophy. The Metachromatic Leukodystrophy companies which have their Metachromatic Leukodystrophy drug candidates in the most advanced stage, i.e. Registered include, Orchard Therapeutics.
Learn more about the emerging Metachromatic Leukodystrophy Pipeline Therapies @ Metachromatic Leukodystrophy Clinical Trials Assessment- https://www.delveinsight.com/sample-request/metachromatic-leukodystrophy-mld-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr
Scope of the Metachromatic Leukodystrophy Pipeline Report
• Coverage- Global
• Metachromatic Leukodystrophy Therapeutic Assessment by Product Type: Mono, Combination, Mono/Combination
• Metachromatic Leukodystrophy Therapeutic Assessment by Clinical Stages: Discovery, Pre-clinical, Phase I, Phase II, Phase III
• Metachromatic Leukodystrophy Companies- Takeda, Denali Therapeutics, Orchard Therapeutics, Homology Medicines, Passage Bio, ArmaGen Technologies, and others.
• Metachromatic Leukodystrophy Pipeline Therapies- SHP611, HGT-1110, OTL-200, rhARSA, MGTA-456, and others.
Dive deep into rich insights for new drugs for Metachromatic Leukodystrophy Treatment, Visit @ Metachromatic Leukodystrophy Market Drivers and Barriers, and Future Perspective- https://www.delveinsight.com/sample-request/metachromatic-leukodystrophy-mld-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr
Table of Content
1. Introduction
2. Executive Summary
3. Metachromatic Leukodystrophy: Overview
4. Pipeline Therapeutics
5. Therapeutic Assessment
6. Metachromatic Leukodystrophy- DelveInsight's Analytical Perspective
7. In-depth Commercial Assessment
8. Metachromatic Leukodystrophy Collaboration Deals
9. Late Stage Products (Phase III)
10. Drug Name: Company Name
11. Drug profiles in the detailed report…..
12. Mid Stage Products (Phase II)
13. TAK-611: Takeda
14. Drug profiles in the detailed report…..
15. Early Stage Products (Phase I)
16. Drug Name: Company Name
17. Drug profiles in the detailed report…..
18. Preclinical and Discovery Stage Products
19. PBML-04: Passage Bio
20. Drug profiles in the detailed report…..
21. Inactive Products
22. Metachromatic Leukodystrophy Key Companies
23. Metachromatic Leukodystrophy Key Products
24. Metachromatic Leukodystrophy- Unmet Needs
25. Metachromatic Leukodystrophy- Market Drivers and Barriers
26. Metachromatic Leukodystrophy- Future Perspectives and Conclusion
27. Metachromatic Leukodystrophy Analyst Views
28. Metachromatic Leukodystrophy Key Companies
29. Appendix
For further information on the Metachromatic Leukodystrophy Pipeline therapeutics, reach out to Metachromatic Leukodystrophy Unmet Needs and Analyst Views- https://www.delveinsight.com/sample-request/metachromatic-leukodystrophy-mld-pipeline-insight?utm_source=openpr&utm_medium=pressrelease&utm_campaign=ypr
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About Us
DelveInsight is a leading healthcare-focused market research and consulting firm that provides clients with high-quality market intelligence and analysis to support informed business decisions. With a team of experienced industry experts and a deep understanding of the life sciences and healthcare sectors, we offer customized research solutions and insights to clients across the globe. Connect with us to get high-quality, accurate, and real-time intelligence to stay ahead of the growth curve.
Company Name: DelveInsight Business Research LLP
Contact Person: Yash Bhardwaj
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